Clinical Studies that Generate real-life Results

Innovative Research Center

Our Research Results in the Next Generation of Treatments

Convenient and Flexible Service

Personal Patient Care

Your comfort and care is our primary mission!

Request Appointment

Clinical Trials Lead to Innovation

Ongoing Clinical Trials

Clinical Trial Validate Great Research for Innovative Treatments

Research Center

Our studies result in better treatments. Ongoing research fuels our best practices for our patients and the greater health of all with lysosomal disorders.

Find Out More

Patient Center

The Lysosomal Center offers comfortable and caring treatment with a wide-range of infusion services at our Northern Virginia offices.

Request Appointment

Clinical Trials

We transform great research into great treatments for all. Testing the efficacy of our work is critical for delivering meaningful results for our patients.

Learn More

Leader in Lysosomal Research

20+ Years of experience

Our experience in research of solutions to lysosomal disorders allows us to offer the best treatments and cutting-edge research that leads to better care.

Outstanding Care

On Your Schedule

Great Research

Over 60 Studies

Our Numbers

Papers Publish

Patients Served

Trials Run

Research, Conferences and Clinical Trial Updates

RARE Newsletter

Stay current with latest research and treatments