Translational Center

Our studies result in better treatments. Ongoing research fuels our best practices for our patients and the greater health of all with lysosomal disorders.

Patient Center

The Lysosomal Center offers comfortable and caring treatment with a wide-range of infusion services at our Northern Virginia offices.

Clinical Trials

We transform great research into great treatments for all. Testing the efficacy of our work is critical for delivering meaningful results for our patients.

Leader in Lysosomal Research

20+ Years of experience

Our experience in research of solutions to lysosomal disorders allows us to offer the best treatments and cutting-edge research that leads to better care.

Our Numbers

Papers Published
Patients Served
Trials Run

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